Autori: Darras BT

Filtra

Data

Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial

2-Year Change in Revised Hammersmith Scale Scores in a Large Cohort of Untreated Paediatric Type 2 and 3 SMA Participants

Revised upper limb module in type II and III spinal muscular atrophy: 24-month changes

Different trajectories in upper limb and gross motor function in spinal muscular atrophy

Age related treatment effect in type II Spinal Muscular Atrophy pediatric patients treated with nusinersen

Nusinersen in pediatric and adult patients with type III spinal muscular atrophy

Respiratory Trajectories in Type 2 and 3 Spinal Muscular Atrophy in the iSMAC Cohort Study

Clinical Variability in Spinal Muscular Atrophy Type III

Gain and loss of abilities in type II SMA: A 12-month natural history study

Longitudinal natural history of type I spinal muscular atrophy: a critical review

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